Trusted Resources: People & Places
Healthcare providers, researchers, and advocates
Marina Cavazzana, MD
Researcher Head
Department of Biotherapy
Hôpital Necker
149 Rue de Sèvres
Paris, France
Marina Cavazzana is a pediatrician, Professor of Haematology since 2000, Head of the Biotherapy Department at Hospital Necker, University Paris Descartes. She is the Director of the Inserm / Assistance Publique – Hôpitaux de Paris GHU Ouest Biotherapy Clinical Investigation Center and leads a research Laboratory at Imagine Institute. She studied medicine in Padua, Italy and received Doctorate of Medicine in 1983, her certification in Paediatrics in 1987 and a PhD in Life Sciences in 1993 (University Paris VII).
Dr. Marina Cavazzana has dedicated her time and research in investigating innovative protocol with a particular intervention gene therapy, focusing on sickle cell disease.
Her main research and clinical interests are development of the immune system, genetic diseases of the haematopoietic system and cell and gene therapy. Her group studies the means to improve the clinical results of hematopoietic stem cell transplantation, crossing HLA-barriers, and the differentiation of mouse and human stem cells towards lymphocyte lineages. She has initiated several clinical trials based on the use of ex vivo gene modified cells to treat patients with inherited disorders, the preliminary clinical results of which are encouraging.
She is the author or co-author of one patent and of more than 270 publications in peer-reviewed journals.
Representative Publications:
Gene Therapy in a Patient with Sickle Cell Disease
Related Content
-
Grant Recipient Uses Mobile Device Observation in Sickle Cell Pain StudyTechnology takes center stage in a new...
-
Webinar Series: Sickle Cell Science: Path to Progress – Genetic Therapies in Sickle Cell DiseaseTo commemorate Sickle Cell Awareness Mon...
-
A systematic review of the literature for severity predictors in pediatric sickle cell anemia patientsBackground: All patients with HbSS (SCA)...
-
Mount Sinai HospitalIn addition to dedicated treatment progr...
-
East Carolina University Comprehensive Sickle Cell CenterEast Carolina University Comprehensive S...
-
Lisa Pullens, RN, BSN, CPHNLisa received her RN-BSN 33 years ago at...