Sickle Cell Disease news and research updates
Research readouts, treatment and access decisions, and community updates for people living with sickle cell disease and the people who care for them — each one dated, with a link to the original source where there is one.
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Sickle Cell Disease Clinical Fellow
Our mission is to train the next generation of providers with expertise in the care of individuals with sickle cell disease (SCD) throughout their lifespan. Objectives: 1. To…
Agios Pharmaceuticals to Present RISE UP Phase 3 Trial Results of Mitapivat in Sickle Cell Disease at EHA 2026 Plenary Session
Agios Pharmaceuticals will present Phase 3 trial results for mitapivat in sickle cell disease at EHA 2026. Quiver AI Summary Agios Pharmaceuticals announced that detailed results…
Newer blood thinners tied to less bleeding in sickle cell disease study
Newer oral anticoagulants, or blood thinners, were linked to a lower risk of clinically relevant nonmajor bleeding than warfarin, an older blood thinner, in adults with sickle…
Beam Therapeutics to Present Updated Biomarker Data from Phase 1/2 BEACON Trial Further Underscoring Risto-cel’s Ability to Restore Red Blood Cell Health and Function in Sickle Cell Disease at EHA2026
CAMBRIDGE, Mass., May 12, 2026 (GLOBE NEWSWIRE) -- Beam Therapeutics Inc. (Nasdaq: BEAM), a biotechnology company developing precision genetic medicines through base editing…
Mitapivat sNDA Seeks FDA Accelerated Approval in Sickle Cell Disease
Key Takeaways Agios aligned with FDA on a 52-week, randomized, double-blind confirmatory trial (n≈159; age ≥12 years) using transfusion-free status from weeks 4–52 as the primary…
Red Blood Cell Exchange in Sickle Cell Disease Care: A Comprehensive Review
ABSTRACT Erythrocytaphoresis or RBC exchange (RBCX) is a key intervention in the management of sickle cell anemia for both chronic prophylaxis and emergent clinical care during…
Sickle cell graduate calls for non-kinetic solutions to tackle insecurity
As insecurity intensifies across the country, Joseph Ifechukwu Agbanyin, a 25-year-old software engineering graduate living with sickle cell anemia, has called on the government…
Hematopoietic Stem Cell Transplantation as Curative Therapy in Sickle Cell Disease
Sickle cell disease (SCD) is a hereditary hemoglobinopathy characterized by chronic hemolytic anemia, recurrent vaso-occlusive crises, progressive organ damage, and reduced life…
4 Hematology Headlines You Missed in April 2026
April 2026 brought major developments in hematology, particularly in sickle cell disease (SCD) , with advances spanning phase 3 therapeutics, gene-editing strategies, pediatric…
Agios Submits sNDA to FDA for U.S. Accelerated Approval of Mitapivat in Sickle Cell Disease
CAMBRIDGE, Mass., May 12, 2026 (GLOBE NEWSWIRE) -- Agios Pharmaceuticals, Inc. (Nasdaq: AGIO), a commercial-stage biopharmaceutical company focused on delivering innovative…
Implementation of third-generation digital PCR for non-invasive prenatal diagnosis of sickle cell disease and early detection. Pilot study
Sickle cell disease (SCD) is one of the most prevalent autosomal recessive conditions worldwide, affecting more than 600,000 newborns annually. Despite advances in treatment, it…
HCT Shows Promising Safety and Efficacy in SCD
HLA-matched sibling donor (MSD) hematopoietic cell transplantation (HCT) done prior to adolescence demonstrated promising safety and efficacy outcomes among patients with sickle…