Sickle Cell Disease news and research updates
Research readouts, treatment and access decisions, and community updates for people living with sickle cell disease and the people who care for them — each one dated, with a link to the original source where there is one.
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FDA reviewing Casgevy for children with sickle cell as young as 5
The U.S. Food and Drug Administration is reviewing an application from Vertex Pharmaceuticals seeking approval of Casgevy (exagamglogene autotemcel) for children with sickle cell…
BNP Paribas Cardif expands its inclusive approach to people with sickle cell anemia
Building on its commitment to make insurance more accessible, especially for those affected by chronic or rare diseases, the insurer BNP Paribas Cardif is introducing new pricing…
Sickle Cell Disease — Global Competitive Landscape Report 2026 | EHA 2026
Sickle Cell Disease is included as an EHA 2026 disease-area keyword under non-malignant hematology, with relevant subtypes including Sickle Cell Pain Crises, Vaso-Occlusive…
Agios Showcases RISE UP Phase 3 Results at EHA 2026 Plenary Session Reinforcing Strong Anti-Hemolytic Profile of Mitapivat in Sickle Cell Disease
Mitapivat demonstrated statistically significant improvement in hemoglobin response compared with placebo, with rapid onset and durable effects New analyses showed patients in…
Mitapivat Improves Anaemia in Sickle Cell Disease: EHA 2026
MITAPIVAT significantly improved haemoglobin levels and markers of haemolysis in patients with sickle cell disease (SCD) in a Phase 3 trial, with additional clinical benefits…
CURRENT CLINICAL TRIALS FOR NEW THERAPIES IN SICKLE CELL DISEASE DO NOT ADEQUATELY REPRESENT THE PATIENT POPULATION
Background: Sickle cell disease (SCD) is a progressive disorder characterized by acute pain crisis (APC), organ damage, and early mortality. Despite the (few) disease-modifying…
Governor Spanberger Signs Queen Candis Act Into Law, First-in-the-Nation Package to Transform Sickle Cell Care
New Laws Will Expand Education, Training, Access, and Coordinated Care for Virginians with Sickle Cell NEWPORT NEWS, VA — Governor Abigail Spanberger today signed a…
Sickle Cell, Thalassaemia and Red Cell Disorder Service
We are a specialist centre for the diagnosis and management of adults with inherited haemoglobin disorders including sickle cell disease, thalassaemia. Who we see We see patients…
Teen with Sickle Cell Disease, Headache and Forehead Swelling
Introduction Sickle cell disease (SCD) is the most common inherited blood disorder in the USA and globally, with a gradual increase in prevalence (1). SCD continues to impose a…
Severe maternal morbidity according to sickle cell disease genotype
Abstract Background Sickle cell disease (SCD) is a genetic hemoglobinopathy that disproportionately affects individuals of African descent and is associated with elevated risks of…
Gene-editing therapy frees first trial participant from SCD symptoms
A patient with severe sickle cell disease (SCD) remained free of two key SCD symptoms — including painful vaso-occlusive crises — for more than a year after receiving a single…
Nonmyeloablative HLA-identical sibling transplant for sickle cell disease in children: a multicenter prospective study
Abstract HLA-identical sibling donor hematopoietic cell transplant (HCT) is an established curative therapy for sickle cell disease (SCD). Although myeloablative HCT conditioning…