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HHS Secretary Alex Azar Touts White House Efforts to Fight Sickle Cell Disease
By 2029, Americans with sickle cell disease (SCD) could be living 10 years longer than they do today, predicts U.S. Health and Human Services Secretary Alex Azar.
That’s one of the Trump administration’s long-term goals, Azar — the nation’s top health official — told more than 900 delegates attending the 2019 NORD Rare Diseases & Orphan Products Breakthrough Summit in Washington, D.C.
The recent summit, organized by the National Organization for Rare Disorders, also featured speeches by Norman E. “Ned” Sharpless, MD, acting commissioner of the U.S. Food and Drug Administration (FDA), and his predecessor, former FDA Commissioner Scott Gottlieb, MD. In his 17-minute speech, Azar used SCD as an example of President Trump’s commitment to those with rare diseases.
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