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The Bill and Melinda Gates Foundation awarded a $1.5 million grant to Boston Children’s Hospital to research and develop gene therapy treatment for sickle cell disease.
The research will be directed toward gene therapy methods that can be applied in developing regions of the world, where sickle cell disease incidence is high.
“While gene therapies are currently confined to a few research hospitals in the U.S. and other developed countries, our long-term goal is to make this treatment available to patients in developing countries — and we have already begun to think about how to translate this specialized, potentially curative therapy,” David A. Williams, MD, chief scientific officer and senior vice president of Boston Children’s Hospital and president of Dana-Farber/Boston Children’s Cancer and Blood Disorders Center, said in a press release.
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This platform is made possible through a partnership with the Sickle Cell Disease Association of America, Inc. (SCDAA) and its member organizations. SCDAA's mission is to advocate for people affected by sickle cell conditions and empower community-based organizations to maximize quality of life and raise public consciousness while advancing the search for a universal cure.