Google
Trusted Resources: News & Events
Latest announcements and gatherings
Pfizer Executive Outlines Vision for Treating Sickle Cell Disease, Other Rare Diseases
Consumers may know Pfizer as the company that manufactures Viagra, but the New York-based pharma giant is investing millions in developing potential treatments and gene therapies for rare disorders ranging from sickle cell disease and hemophilia to ALS and Duchenne muscular dystrophy.
Michael Wajnrajch, MD, is senior medical director for Pfizer’s Rare Disease Group and pediatric endocrinologist on the faculty of New York University. Wajnrajch outlined his company’s vision for gene therapies at the 2nd International Congress on Advanced Treatments in Rare Diseases, held March 4-5 in Vienna, Austria.
“Sometimes we’re doing the right thing for the right reasons, and it’s not about the money,” he told some 100 delegates. “Sickle cell disease predominantly affects patients with very limited ability to pay. We’re not going to make much money on this, but we know it’s an unmet medical need in many parts of the world.”
+myBinderRelated Content
-
The first South American case of pre-implantation genetic diagnosis to select compatible embryo for cord blood trans...Sickle cell anemia is an inherited syste...
-
Mandy DavidMandy David is a senior health communica...
-
Angela Rivers, MD, PhDDr. Rivers is the Director at Sickle Cel...
-
Screening for sickle cell and beta thalassaemiaSickle cell and beta thalassaemi...
-
Boston public schools agree to recognize sickle cell disease as disabilityThe Boston school system has agreed to r...
-
Estimated pulmonary artery systolic pressure and sickle cell disease: a meta-analysis and systematic reviewMany studies report estimated pulmonary ...
-
Could Gene Therapy Cure Sickle Cell Anemia?Nearly 20 years ago, scientists stunned ...
To improve your experience on this site, we use cookies. This includes cookies essential for the basic functioning of our website, cookies for analytics purposes, and cookies enabling us to personalize site content. By clicking on 'Accept' or any content on this site, you agree that cookies can be placed. You may adjust your browser's cookie settings to suit your preferences. More Information
The cookie settings on this website are set to "allow cookies" to give you the best browsing experience possible. If you continue to use this website without changing your cookie settings or you click "Accept" below then you are consenting to this.
Powered by
Support for this site is provided by
This platform is made possible through a partnership with the Sickle Cell Disease Association of America, Inc. (SCDAA) and its member organizations. SCDAA's mission is to advocate for people affected by sickle cell conditions and empower community-based organizations to maximize quality of life and raise public consciousness while advancing the search for a universal cure.