Which Treatment Is Right for Me or My Child?

Overview of Presentation: • Background: Timeline of Therapies in SCD • Background: Complications in Sickle Cell Disease • Review of current disease modifying therapies and clinical trials • Review of new mechanisms of action for new disease modifying therapies • Considerations and Clinical Scenarios for therapies in SCD • Review current FDA approved treatments and Curative therapies Future for new Therapies Are Bright for SCD! • There are over 20 new therapeutic products under investigation for SCD • These include Bone Marrow Transplant and Gene Therapies   Abstract source