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Clinical Trials: The Patient Experience
The FDA’s Center for Biologics Evaluation and Research (CBER) Office of Therapeutic Products (OTP) is hosting a public virtual workshop on Thursday, April 13, from 11:00 a.m. – 3:00 p.m. ET.
The workshop, Clinical Trials: The Patient Experience, will feature a panel of rare disease patients, caregivers, and advocates who will share their experiences with gene therapy clinical trials. Through participation in clinical trials, patients can help advance the science of gene therapy and further the development of rare disease treatments.
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